| ETFDH |
231680 |
Musculoskeletal-diseases |
|
musculoskeletal |
#12815589 #15669683 |
| ETFDH |
231680 |
Bone-diseases |
|
musculoskeletal |
#15669683 |
| ETFDH |
231680 |
Spinal-diseases |
scoliosis
|
musculoskeletal |
15669683 |
| ETFDH |
231680 |
Muscular-diseases |
proximal myopathy; lipid storage myopathy; intercostal muscles impaired
|
musculoskeletal |
12815589 15669683 |
| ETFDH |
231680 |
Craniofacial-abnormalities |
|
musculoskeletal |
#12815589 |
| ETFDH |
231680 |
Macrocephaly |
enlarged head
|
musculoskeletal |
12815589 |
| ETFDH |
231680 |
Digestive-system-diseases |
|
gastrointestinal |
#10356148 #12815589 #15662686 #15669683 |
| ETFDH |
231680 |
Biliary-tract-diseases |
|
gastrointestinal |
#12815589 |
| ETFDH |
231680 |
Cholestasis |
bile duct hypoplasia
|
gastrointestinal |
12815589 |
| ETFDH |
231680 |
Liver-diseases |
|
gastrointestinal |
#12815589 #15662686 #15669683 |
| ETFDH |
231680 |
Fatty-liver |
fatty degeneration; siderosis; steatosis
|
gastrointestinal |
12815589 15669683 |
| ETFDH |
231680 |
Hepatomegaly |
|
gastrointestinal |
12815589 15662686 15669683 |
| ETFDH |
231680 |
Vomiting |
nausea
|
gastrointestinal |
10356148 12815589 |
| ETFDH |
231680 |
Respiratory-tract-diseases |
|
respiratory |
#10356148 #12815589 #15662686 #15669683 |
| ETFDH |
231680 |
Lung-diseases |
|
respiratory |
#12815589 |
| ETFDH |
231680 |
Pulmonary-hypoplasia |
|
respiratory |
12815589 |
| ETFDH |
231680 |
Respiration-disorders |
|
respiratory |
#10356148 #12815589 #15662686 #15669683 |
| ETFDH |
231680 |
Hyperventilation |
tachypnea
|
respiratory |
15662686 15669683 |
| ETFDH |
231680 |
Respiratory-insufficiency |
respiratory distress; respiratory arrest; cyanosis; central apnea; hypoventilation; nonobstructive hypoventilation; apneic
|
respiratory |
10356148 12815589 15669683 |
| ETFDH |
231680 |
Nervous-system-diseases |
|
neurologic |
#10356148 #12815589 #15662686 #15669683 |
| ETFDH |
231680 |
Central-nervous-system-diseases |
|
neurologic |
#10356148 #12815589 #15669683 |
| ETFDH |
231680 |
Brain-diseases |
|
neurologic |
#10356148 #12815589 #15669683 |
| ETFDH |
231680 |
Seizures |
episodic seizures
|
neurologic |
12815589 |
| ETFDH |
231680 |
Headache-disorders |
morning headaches; headache
|
neurologic |
10356148 15669683 |
| ETFDH |
231680 |
Cortical-dysplasia |
pachygyria cerebral; cortex abnormal; cortical plate abnormal; neuronal migration abnormal
|
neurologic |
12815589 |
| ETFDH |
231680 |
Neurologic-manifestations |
|
neurologic |
#10356148 #12815589 #15662686 #15669683 |
| ETFDH |
231680 |
Neurobehavioral-manifestations |
|
neurologic |
#12815589 #15669683 |
| ETFDH |
231680 |
Developmental-delay |
motor development
|
neurologic |
15669683 |
| ETFDH |
231680 |
Lethargy |
episodes; recurrent
|
neurologic |
12815589 15669683 |
| ETFDH |
231680 |
Neuromuscular-manifestations |
|
neurologic |
#10356148 #12815589 #15662686 #15669683 |
| ETFDH |
231680 |
Muscle-hypotonia |
muscular hypotonia
|
neurologic |
10356148 12815589 15662686 15669683 |
| ETFDH |
231680 |
Muscle-weakness |
respiratory muscles; infection triggered
|
neurologic |
10356148 12815589 15662686 15669683 |
| ETFDH |
231680 |
Muscular-atrophy |
muscle hypotrophy; limb girdle like
|
neurologic |
15662686 |
| ETFDH |
231680 |
Electromyography-abnormal |
myopathic; chronic; fiber loss
|
neurologic |
15669683 |
| ETFDH |
231680 |
Genitourinary-diseases |
|
genitourinary |
#7912128 #12359134 #12815589 |
| ETFDH |
231680 |
Urologic-diseases |
|
genitourinary |
#7912128 #12359134 #12815589 |
| ETFDH |
231680 |
Kidney-diseases |
|
genitourinary |
#7912128 #12359134 #12815589 |
| ETFDH |
231680 |
Cystic-kidney-diseases |
polycystic kidneys; renal cortical cysts; renal cystic dysplasia; enlarged kidneys; hyperechoic kidneys
|
genitourinary |
7912128 12359134 12815589 |
| ETFDH |
231680 |
Renal-fatty-infiltration |
renal tubular epithelium
|
genitourinary |
12359134 |
| ETFDH |
231680 |
Cardiovascular-diseases |
|
cardiovascular |
#10356148 #12815589 |
| ETFDH |
231680 |
Heart-diseases |
|
cardiovascular |
#12815589 |
| ETFDH |
231680 |
Cardiomyopathy |
myocardium steatosis
|
cardiovascular |
12815589 |
| ETFDH |
231680 |
Cardiorespiratory-arrest |
respiratory arrest; cardiac arrest
|
cardiovascular |
10356148 12815589 |
| ETFDH |
231680 |
Metabolic-diseases |
|
metabolic |
#7912128 #10356148 #12359134 #12815589 #15662686 #15669683 |
| ETFDH |
231680 |
Acid-base-imbalance |
|
metabolic |
#7912128 #10356148 #12815589 #15662686 #15669683 |
| ETFDH |
231680 |
Acidosis |
lactic acidosis
|
metabolic |
7912128 10356148 12815589 15662686 15669683 |
| ETFDH |
231680 |
Glucose-metabolism-disorders |
|
metabolic |
#7912128 #10356148 #12359134 #12815589 #15662686 |
| ETFDH |
231680 |
Hypoglycemia |
episodes; hypoketotic hypoglycemia
|
metabolic |
7912128 10356148 12359134 12815589 15662686 |
| ETFDH |
231680 |
Aminoaciduria |
generalized; glutaricaciduria
|
metabolic |
12815589 |
| ETFDH |
231680 |
Acylcarnitine-profile-abnormal |
elevated C4 acylcarnitine; elevated C5 acylcarnitine; elevated C6 acylcarntine; elevated C12 acylcarnitine
|
metabolic |
10356148 15669683 |
| ETFDH |
231680 |
Acylglycine-profile-abnormal |
acylglycinuria; isovalerylglycinuria
|
metabolic |
7912128 |
| ETFDH |
231680 |
Carnitine-levels-abnormal |
decreased total carnitine; decreased free carnitine; elevated esterified carnitine; secondary carnitine deficiency
|
metabolic |
10356148 15669683 |
| ETFDH |
231680 |
Fatty-acids-abnormal |
myristate oxidation abnormal; palmitate oxidation abnormal; fibroblasts; high free fatty acids
|
metabolic |
10356148 12815589 |
| ETFDH |
231680 |
Organic-acids-abnormal |
ethylmalonic aciduria; glutaric aciduria; butyric aciduria; methylbutyric aciduria; isobutyric aciduria; isovaleric aciduria; propionic aciduria; dicarboxylic aciduria; 2 hydroxyglutaric aciduria; 3 hydroxyisovaleric aciduria; 2 hydroxyisocaproic aciduria; 5 hydroxyhexanoic aciduria
|
metabolic |
10356148 #12359134 12815589 15662686 15669683 |
| ETFDH |
231680 |
Dicarboxylic-aciduria |
dicarboxylic acids elevated
|
metabolic |
10356148 15669683 |
| ETFDH |
231680 |
Ethylmalonic-aciduria |
ethylmalonic acid elevated; ethylmalonate elevated
|
metabolic |
12815589 15662686 15669683 |
| ETFDH |
231680 |
Glutaric-aciduria |
glutaric acid elevated; glutaric acidemia
|
metabolic |
10356148 12359134 12815589 15662686 15669683 |
| ETFDH |
231680 |
Body-temperature-changes |
|
miscellaneous |
#12815589 |
| ETFDH |
231680 |
Fever |
fever triggered; disease onset
|
miscellaneous |
12815589 |
| ETFDH |
231680 |
Dysmorphism-and-abnormalities |
facial dysmorphism; flat nasal bridge; large anterior fontanel; malformed ears; telecanthus; high forehead; prominent forehead; potter face
|
miscellaneous |
12815589 |
| ETFDH |
231680 |
Odors |
sweaty feet; stale breath
|
miscellaneous |
12815589 |
| ETFDH |
231680 |
Creatine-kinase-abnormal |
|
miscellaneous |
15669683 |
| ETFDH |
231680 |
Vitamin-responsive |
riboflavin; vitamin B2; response variable
|
miscellaneous |
3930843 10356148 15669683 |