| HADHB |
609015 |
Musculoskeletal-diseases |
|
musculoskeletal |
#9259266 #9305349 #12548384 #12754706 #15617873 #15902556 #16423905 |
| HADHB |
609015 |
Muscular-diseases |
skeletal myopathy; myopathy; cytoplasmic fatty infiltrations
|
musculoskeletal |
9259266 #9305349 12548384 12754706 15617873 15902556 16423905 |
| HADHB |
609015 |
Rhabdomyolysis |
episodes
|
musculoskeletal |
15617873 15902556 |
| HADHB |
609015 |
Myoglobinuria |
recurrent; progressive
|
musculoskeletal |
9305349 12754706 |
| HADHB |
609015 |
Digestive-system-diseases |
|
gastrointestinal |
#9259266 #12548384 #12754706 #15243991 #15617873 #15902556 #16423905 |
| HADHB |
609015 |
Gastrointestinal-diseases |
|
gastrointestinal |
#15617873 |
| HADHB |
609015 |
Intestinal-obstruction |
intestinal pseudo obstruction; constipation; abdominal distention; dilated loops of small and large intestine
|
gastrointestinal |
15617873 |
| HADHB |
609015 |
Liver-diseases |
hepatic failure
|
gastrointestinal |
9259266 #12548384 15902556 #16423905 |
| HADHB |
609015 |
Fatty-liver |
hepatic steatosis; hepatic fatty infiltration
|
gastrointestinal |
12548384 |
| HADHB |
609015 |
Liver-enzymes-abnormal |
transaminases elevated; mildly elevated
|
gastrointestinal |
16423905 |
| HADHB |
609015 |
Abdominal-pain |
abdominal distension; lower abdominal pain
|
gastrointestinal |
15617873 |
| HADHB |
609015 |
Feeding-difficulties |
feeding impaired
|
gastrointestinal |
12754706 15243991 16423905 |
| HADHB |
609015 |
Vomiting |
episodes
|
gastrointestinal |
15617873 |
| HADHB |
609015 |
Respiratory-tract-diseases |
|
respiratory |
#12548384 #12754706 #15902556 #16423905 |
| HADHB |
609015 |
Lung-diseases |
|
respiratory |
#16423905 |
| HADHB |
609015 |
Pneumonia |
bronchopneumonia; pneumonia suspected based on radiologic examination
|
respiratory |
16423905 |
| HADHB |
609015 |
Pulmonary-edema |
hyaline membrane disease
|
respiratory |
16423905 |
| HADHB |
609015 |
Respiration-disorders |
|
respiratory |
#12548384 #12754706 #15902556 #16423905 |
| HADHB |
609015 |
Hyperventilation |
tachypnea
|
respiratory |
16423905 |
| HADHB |
609015 |
Respiratory-insufficiency |
respiratory distress; acute respiratory distress; bronchiolitis; dyspnea; hypoventilation; shortness of breath
|
respiratory |
12548384 12754706 15902556 16423905 |
| HADHB |
609015 |
Nervous-system-diseases |
|
neurologic |
#9259266 #12548384 #12754706 #15617873 #15902556 #16423905 |
| HADHB |
609015 |
Central-nervous-system-diseases |
|
neurologic |
#9259266 #15902556 |
| HADHB |
609015 |
Brain-diseases |
|
neurologic |
#9259266 #15902556 |
| HADHB |
609015 |
Encephalopathy |
hepatic; acute
|
neurologic |
9259266 15902556 |
| HADHB |
609015 |
Axonal-degeneration |
biopsie finding; axonal degeneration; myelin degeneration
|
neurologic |
12754706 |
| HADHB |
609015 |
Neurologic-manifestations |
|
neurologic |
#12548384 #12754706 #15617873 #15902556 #16423905 |
| HADHB |
609015 |
Ataxia |
mils; ataxic
|
neurologic |
15902556 |
| HADHB |
609015 |
Gait-disorders |
frequent falling
|
neurologic |
15902556 |
| HADHB |
609015 |
Neurobehavioral-manifestations |
|
neurologic |
#12754706 |
| HADHB |
609015 |
Developmental-delay |
milestones delayed; infection triggered
|
neurologic |
12754706 15902556 |
| HADHB |
609015 |
Lethargy |
|
neurologic |
12754706 |
| HADHB |
609015 |
Neuromuscular-manifestations |
|
neurologic |
#12548384 #12754706 #15617873 #15902556 #16423905 |
| HADHB |
609015 |
Muscle-hypotonia |
muscular hypotonia
|
neurologic |
12548384 16423905 |
| HADHB |
609015 |
Muscle-weakness |
lower extremities; diaphragm weakness; skeletal muscle weakness
|
neurologic |
12754706 15617873 15902556 |
| HADHB |
609015 |
Muscular-atrophy |
muscle fiber atrophy; denervating process
|
neurologic |
12754706 |
| HADHB |
609015 |
Muscle-aching-and-stiffness |
muscle pain; episodes
|
neurologic |
12754706 |
| HADHB |
609015 |
Peripheral-nervous-system-diseases |
|
neurologic |
#12754706 #15617873 #15902556 |
| HADHB |
609015 |
Polyneuropathies |
lower extremities; upper extremities; sensorimotor neuropathy; axonopathy; neuropathy
|
neurologic |
12754706 15617873 15902556 |
| HADHB |
609015 |
Eye-diseases |
|
ophthalmologic |
#15902556 |
| HADHB |
609015 |
Retinal-diseases |
retinitis pigmentosa; mild
|
ophthalmologic |
15902556 |
| HADHB |
609015 |
Genitourinary-diseases |
|
genitourinary |
#12548384 #12754706 |
| HADHB |
609015 |
Female-genital-diseases |
|
genitourinary |
#12548384 #12754706 |
| HADHB |
609015 |
Pregnancy-complications |
hypertension or hemolysis elevated liver enzymes and low platelets; HELLP syndrome; hydrothoraces; hydrops generalisatus
|
genitourinary |
12548384 12754706 |
| HADHB |
609015 |
Cardiovascular-diseases |
|
cardiovascular |
#9259266 #10577999 #12548384 #12754706 #15243991 #15902556 #16423905 |
| HADHB |
609015 |
Heart-diseases |
|
cardiovascular |
#9259266 #10577999 #12548384 #12754706 #15243991 #15902556 #16423905 |
| HADHB |
609015 |
Arrhythmia |
conduction impairment; atrial tachycardias
|
cardiovascular |
10577999 |
| HADHB |
609015 |
Cardiomyopathy |
hypertrophic; myocardial hypertrophy; dilated; myocardial fibrosis; ventricular hypertrophy
|
cardiovascular |
9259266 12548384 12754706 15243991 15902556 16423905 |
| HADHB |
609015 |
Cardiorespiratory-arrest |
sudden infant death; cardiorespiratory failure; neonatal form
|
cardiovascular |
9259266 12548384 12754706 15243991 16423905 |
| HADHB |
609015 |
Metabolic-diseases |
|
metabolic |
#9305349 #11855930 #12548384 #12754706 #12838198 #15243991 #15617873 #15902556 #16423905 |
| HADHB |
609015 |
Acid-base-imbalance |
|
metabolic |
#9305349 #12548384 #12754706 #12838198 #16423905 |
| HADHB |
609015 |
Acidosis |
lactic acidosis; metabolic acidosis
|
metabolic |
12548384 12754706 16423905 |
| HADHB |
609015 |
Hypoketosis |
hypoketotic hypoglycemia; deficient fasting ketogenesis
|
metabolic |
9305349 12548384 12754706 12838198 16423905 |
| HADHB |
609015 |
Metabolic-brain-diseases |
|
metabolic |
#12754706 #15243991 #16423905 |
| HADHB |
609015 |
Reye-like-symptoms |
reye syndrome like
|
metabolic |
12754706 15243991 16423905 |
| HADHB |
609015 |
Glucose-metabolism-disorders |
|
metabolic |
#12548384 #12754706 #15243991 #15617873 |
| HADHB |
609015 |
Hypoglycemia |
recurrent; infantile; hypoketotic hypoglycemia; hypoglycaemia
|
metabolic |
12548384 12754706 15243991 15617873 |
| HADHB |
609015 |
Acylcarnitine-profile-abnormal |
plasma; blood spots; elevated 3 hydroxy acylcarnitines; elevated 3 hydroxy C16:0 C16:1 C18:1 C18:2 acylcarnitines; elevated tetradecenoylcarnitine; elevated hexadecenoylcarnitine
|
metabolic |
11855930 12548384 12838198 15243991 15902556 16423905 |
| HADHB |
609015 |
Carnitine-levels-abnormal |
decreased total carnitine; decreased free carnitine; elevated esterified carnitine
|
metabolic |
9305349 |
| HADHB |
609015 |
Organic-acids-abnormal |
lactic aciduria; dicarboxylic aciduria; 3 hydroxydicarboxylic aciduria
|
metabolic |
9305349 12838198 15902556 16423905 |
| HADHB |
609015 |
Dicarboxylic-aciduria |
dicarboxylic acids elevated
|
metabolic |
9305349 12838198 15902556 16423905 |
| HADHB |
609015 |
Immune-system-diseases |
|
immunologic |
#12548384 #12754706 #15902556 |
| HADHB |
609015 |
Infections |
recurrent; intercurrent; viral infections; respiratory tract infections
|
immunologic |
12548384 12754706 15902556 |
| HADHB |
609015 |
Edema |
generalized edema; severe
|
miscellaneous |
16423905 |
| HADHB |
609015 |
Exercise-intolerance |
fatigue; stair climbing abnormal; standing up abnormal
|
miscellaneous |
12754706 15902556 |
| HADHB |
609015 |
Growth-disorders |
|
miscellaneous |
#15617873 |
| HADHB |
609015 |
Failure-to-thrive |
|
miscellaneous |
15617873 |
| HADHB |
609015 |
Mitochondria-abnormal |
subsarcolemmal accumulation of mitochondria
|
miscellaneous |
15902556 |
| HADHB |
609015 |
Creatine-kinase-abnormal |
elevated
|
miscellaneous |
12548384 12754706 |