| MLYCD |
248360 |
Musculoskeletal-diseases |
|
musculoskeletal |
#12955715 |
| MLYCD |
248360 |
Craniofacial-abnormalities |
|
musculoskeletal |
#12955715 |
| MLYCD |
248360 |
Macrocephaly |
progressive
|
musculoskeletal |
12955715 |
| MLYCD |
248360 |
Digestive-system-diseases |
|
gastrointestinal |
#3709568 #6145813 #8259873 #9177981 #9869665 #10417274 #12955715 #16275149 |
| MLYCD |
248360 |
Gastrointestinal-diseases |
|
gastrointestinal |
#6145813 |
| MLYCD |
248360 |
Intestinal-obstruction |
constipation; chronic constipation
|
gastrointestinal |
6145813 |
| MLYCD |
248360 |
Liver-diseases |
|
gastrointestinal |
#12955715 |
| MLYCD |
248360 |
Fatty-liver |
liver fatty infiltration
|
gastrointestinal |
12955715 |
| MLYCD |
248360 |
Liver-enzymes-abnormal |
AST elevated; ALT elevated
|
gastrointestinal |
12955715 |
| MLYCD |
248360 |
Hepatomegaly |
|
gastrointestinal |
12955715 |
| MLYCD |
248360 |
Abdominal-pain |
|
gastrointestinal |
6145813 |
| MLYCD |
248360 |
Feeding-difficulties |
feeding tube; poor feeding; anorexia; food refusal
|
gastrointestinal |
9177981 9869665 12955715 16275149 |
| MLYCD |
248360 |
Diarrhea |
|
gastrointestinal |
9177981 |
| MLYCD |
248360 |
Vomiting |
episodes of vomiting; recurrent
|
gastrointestinal |
3709568 6145813 8259873 9177981 10417274 |
| MLYCD |
248360 |
Respiratory-tract-diseases |
|
respiratory |
#9177981 #9869665 |
| MLYCD |
248360 |
Respiration-disorders |
poor respirations
|
respiratory |
#9177981 9869665 |
| MLYCD |
248360 |
Hyperventilation |
tachypnea; rapid breathing
|
respiratory |
9177981 |
| MLYCD |
248360 |
Nervous-system-diseases |
|
neurologic |
#3709568 #6145813 #7609455 #8259873 #9177981 #9869665 #10417274 #11461195 #11550227 #12955715 #16275149 |
| MLYCD |
248360 |
Central-nervous-system-diseases |
|
neurologic |
#3709568 #7609455 #8259873 #9177981 #10417274 #12955715 #16275149 |
| MLYCD |
248360 |
Brain-diseases |
|
neurologic |
#3709568 #7609455 #8259873 #9177981 #10417274 #12955715 #16275149 |
| MLYCD |
248360 |
Encephalopathy |
diffuse
|
neurologic |
9177981 |
| MLYCD |
248360 |
Cerebrovascular-disorders |
|
neurologic |
#9177981 #12955715 |
| MLYCD |
248360 |
Intracranial-hemorrhages |
cerebral hemorrhage; cerebral infarction
|
neurologic |
9177981 12955715 |
| MLYCD |
248360 |
Seizures |
convulsions; febrile convulsions; afebrile seizures
|
neurologic |
3709568 7609455 8259873 10417274 12955715 |
| MLYCD |
248360 |
Leukoencephalopathy |
MRI findings; white matter abnormal; white matter signals altered; white matter loss
|
neurologic |
12955715 16275149 |
| MLYCD |
248360 |
Cerebral-atrophy |
generalized; cerebral atrophy
|
neurologic |
16275149 |
| MLYCD |
248360 |
Cortical-dysplasia |
pachygyria cerebral; heterotopia; nodular heterotopia; thickened cortex; cortical malformation
|
neurologic |
16275149 |
| MLYCD |
248360 |
Electroencephalogram-abnormal |
diffuse; irregular activity; sharp waves
|
neurologic |
9177981 |
| MLYCD |
248360 |
Neuronal-loss-and-lesions |
MRI findings; white matter abnormal; white matter loss
|
neurologic |
12955715 16275149 |
| MLYCD |
248360 |
Axonal-degeneration |
chronic axonal degeneration
|
neurologic |
12955715 |
| MLYCD |
248360 |
Neurologic-manifestations |
|
neurologic |
#7609455 #9869665 #11550227 #12955715 #16275149 |
| MLYCD |
248360 |
Neurobehavioral-manifestations |
|
neurologic |
#16275149 |
| MLYCD |
248360 |
Developmental-delay |
psychomotor retardation; neurodevelopment delayed
|
neurologic |
3709568 6145813 7609455 8259873 9177981 9869665 10417274 11461195 11550227 12955715 16275149 |
| MLYCD |
248360 |
Irritability |
irritable
|
neurologic |
16275149 |
| MLYCD |
248360 |
Neuromuscular-manifestations |
|
neurologic |
#7609455 #9869665 #11550227 #12955715 #16275149 |
| MLYCD |
248360 |
Muscle-spasticity |
mild spasticity
|
neurologic |
16275149 |
| MLYCD |
248360 |
Muscle-hypotonia |
generalized
|
neurologic |
7609455 9869665 11550227 12955715 |
| MLYCD |
248360 |
Reflexes-abnormal |
|
neurologic |
#12955715 |
| MLYCD |
248360 |
Pyramidal-tract-signs |
lower extremities
|
neurologic |
12955715 |
| MLYCD |
248360 |
Genitourinary-diseases |
|
genitourinary |
#9869665 #12955715 |
| MLYCD |
248360 |
Urogenital-abnormalities |
|
genitourinary |
#12955715 |
| MLYCD |
248360 |
Hypospadias |
|
genitourinary |
12955715 |
| MLYCD |
248360 |
Urologic-diseases |
|
genitourinary |
#9869665 |
| MLYCD |
248360 |
Kidney-diseases |
renal dysplasia
|
genitourinary |
9869665 |
| MLYCD |
248360 |
Cardiovascular-diseases |
|
cardiovascular |
#7609455 #9177981 #9869665 #10417274 #11461195 #11550227 #12955715 |
| MLYCD |
248360 |
Heart-diseases |
|
cardiovascular |
#7609455 #9177981 #9869665 #10417274 #11461195 #11550227 #12955715 |
| MLYCD |
248360 |
Cardiomyopathy |
hypertrophic; dilatative; left ventricle dilatation; cardiomegaly; myocardium thickening
|
cardiovascular |
7609455 9177981 9869665 10417274 11461195 11550227 12955715 |
| MLYCD |
248360 |
Cardiorespiratory-arrest |
cardiac arrest; cardiogenic shock; cardiac failure
|
cardiovascular |
9177981 9869665 11461195 12955715 |
| MLYCD |
248360 |
Hematologic-diseases |
|
hematologic |
#12955715 |
| MLYCD |
248360 |
Blood-coagulation-disorders |
prothrombin time prolonged
|
hematologic |
12955715 |
| MLYCD |
248360 |
Metabolic-diseases |
|
metabolic |
#3709568 #6145813 #7609455 #8259873 #9177981 #9869665 #10417274 #11461195 #11550227 #12955715 #16275149 |
| MLYCD |
248360 |
Acid-base-imbalance |
|
metabolic |
#3709568 #6145813 #9177981 #10417274 #12955715 #16275149 |
| MLYCD |
248360 |
Acidosis |
metabolic acidosis; lactic acidosis; blood; CSF
|
metabolic |
3709568 6145813 9177981 10417274 12955715 16275149 |
| MLYCD |
248360 |
Glucose-metabolism-disorders |
|
metabolic |
#3709568 #9177981 #10417274 #12955715 |
| MLYCD |
248360 |
Hypoglycemia |
|
metabolic |
3709568 9177981 10417274 12955715 |
| MLYCD |
248360 |
Hyperammonemia |
ammonia levels elevated
|
metabolic |
16275149 |
| MLYCD |
248360 |
Acylcarnitine-profile-abnormal |
malonylcarnitine elevated; propionylcarnitin elevated
|
metabolic |
7609455 9177981 12955715 16275149 |
| MLYCD |
248360 |
Carnitine-levels-abnormal |
decreased total carnitine; decreased free carnitine; elevated esterified carnitine
|
metabolic |
7609455 12955715 |
| MLYCD |
248360 |
Fatty-acids-abnormal |
myristic acids abnormal; palmitic acids abnormal; fatty acids oxidation abnormal; triglyceride levels elevated
|
metabolic |
6145813 11461195 |
| MLYCD |
248360 |
Organic-acids-abnormal |
malonic aciduria; methylmalonic aciduria; fumaric aciduria; 3 hydroxypropionate uria; malate uria; dicarboxylic aciduria; glutaric aciduria; 3 methylglutaconic acids elevated
|
metabolic |
3709568 6145813 7609455 8259873 9177981 9869665 10417274 11461195 11550227 12955715 16275149 |
| MLYCD |
248360 |
Dicarboxylic-aciduria |
dicarboxylic acids elevated
|
metabolic |
3709568 9177981 |
| MLYCD |
248360 |
Glutaric-aciduria |
|
metabolic |
3709568 9177981 |
| MLYCD |
248360 |
Methylglutaconic-aciduria |
3 methylglutaconic acids elevated
|
metabolic |
11461195 |
| MLYCD |
248360 |
Methylmalonic-aciduria |
methylmalonic acid elevated
|
metabolic |
3709568 6145813 7609455 9177981 10417274 11461195 12955715 16275149 |
| MLYCD |
248360 |
TCA-intermediates-elevated |
tricarboxylic acid cycle intermediates elevated
|
metabolic |
3709568 |
| MLYCD |
248360 |
Splenomegaly |
hepatosplenomegaly
|
miscellaneous |
12955715 |
| MLYCD |
248360 |
Growth-disorders |
|
miscellaneous |
#6145813 #10417274 #12955715 #16275149 |
| MLYCD |
248360 |
Failure-to-thrive |
|
miscellaneous |
12955715 16275149 |
| MLYCD |
248360 |
Growth-deficiency |
short stature
|
miscellaneous |
6145813 10417274 12955715 16275149 |
| MLYCD |
248360 |
Dysmorphism-and-abnormalities |
craniofacial dysmorphism; cranial dysmorphism; facial dysmorphism; micropenis; urogenital abnormalities; renal dysplasia
|
miscellaneous |
9869665 11461195 12955715 |
| MLYCD |
248360 |
Creatine-kinase-abnormal |
elevated
|
miscellaneous |
12955715 |
| MLYCD |
248360 |
Carnitine-responsive |
|
miscellaneous |
7609455 12955715 |